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龐貝氏症市場，按給藥途徑、最終用途、治療類型、國家和地區 - 2023-2030 年行業分析、市場規模、市場佔有率和預測

市場調查報告書

商品編碼

1351405

龐貝氏症市場，按給藥途徑、最終用途、治療類型、國家和地區 - 2023-2030 年行業分析、市場規模、市場佔有率和預測

Pompe Disease Market, By Route of Administration, By End-Use, By Treatment Type, By Country, and By Region - Industry Analysis, Market Size, Market Share & Forecast from 2023-2030

出版日期: 2023年08月01日 | 出版商:

AnalystView Market Insights | 英文 290 Pages | 商品交期: 2-3個工作天內

價格

簡介目錄圖表

報告要點

2022 年龐貝氏症市場規模為 13.2223 億美元，2023 年至 2030 年年複合成長率為 4.2%。

龐貝氏症市場 - 市場動態：

製藥公司、研究機構和患者權益團體之間不斷加強合作，以推動市場需求
致力於龐貝氏症患者的製藥公司、學術機構和倡導組織之間不斷加強的合作極大地推動了龐貝氏症研究和治療的進步。這種協作協同作用促進了知識、專業知識和資源的交流，從而加快了創新療法的發現。監管機構提供獎勵措施和孤兒藥稱號，以激勵公司投資於罕見疾病研究。此外，患者權益團體透過提高公眾意識和組織籌款活動為研究和臨床試驗籌集資金，發揮關鍵作用。這項集體努力增強了我們對該疾病根本原因的了解，並為個人化治療的發展鋪平了道路，最終改善了龐貝氏症患者的預後和生活品質。

龐貝氏症市場 - 主要見解：

我們的研究分析師估計，在2023 年至2030 年的預測期內，全球龐貝氏症市場的年複合成長率預計約為4.2%。這一預期成長歸因於製藥公司、研究機構和患者計劃之間不斷加強的合作小組，顯示推進龐貝氏症研究和治療的正面趨勢。
全球龐貝氏症市場根據各種因素進行分類，包括給藥途徑、最終用途和地區。
在給藥途徑類別中，腸外給藥在 2022 年成為主導部分。這表明在治療龐貝氏症時對這種給藥方式的顯著偏好。
在最終用途細分方面，醫院在 2022 年處於領先地位。這表明醫院在為龐貝病患者提供醫療護理和治療方面發揮著至關重要的作用。
此外，北美成為 2022 年不同地區的主要收入來源。

龐貝氏症市場-細分分析：

全球龐貝氏症市場根據各種因素進行細分，包括給藥途徑、最終用途、治療類型和地區。
在給藥途徑確定的類別中，注射劑領域佔據市場主導地位。這顯示在治療龐貝氏症（一種罕見的遺傳性疾病）時普遍偏好腸外治療。透過靜脈注射進行酵素替代療法（ERT）在疾病管理中發揮關鍵作用。這種療法直接輸送缺乏的酶，有效解決細胞內肝醣累積的問題，進而改善受影響個體的肌肉功能。

龐貝氏症市場-競爭格局：

龐貝氏症研究和治療領域的特點是製藥公司、研究機構和倡導團體之間的動態交互作用。與學術組織的合作促進了科學進步，而患者倡導團體在提高意識、資助研究工作和倡導監管支持方面發揮關鍵作用。孤兒藥資格進一步激勵了該領域的競爭。在這個競爭環境中，公司透過強調治療效果、可及性和患者支持計劃的實施來努力使自己脫穎而出。這項競賽是加速進步的催化劑，帶來更廣泛的治療選擇，並全面提高為龐貝氏症患者提供的照護品質。

介紹
- 按地理位置分類的細分市場佔有率分析
北美洲
- 概述
- 龐貝氏症北美主要製造商
- 北美市場規模和預測（按國家）
- 北美市場規模與預測（按管理途徑）
- 北美市場規模和預測（按治療類型）
- 北美市場規模和預測（按最終用戶）
- 美國
- 加拿大
歐洲
- 概述
- 龐貝氏病歐洲主要製造商
- 歐洲市場規模和預測（按國家）
- 歐洲市場規模與預測（按管理途徑）
- 歐洲市場規模和預測（按治療類型）
- 歐洲市場規模和預測（按最終用戶）
- 德國
- 義大利
- 英國
- 法國
- 俄羅斯
- 荷蘭
- 瑞典
- 波蘭
- 歐洲其他地區
亞太地區 (APAC)
- 概述
- 龐貝氏症亞太地區主要製造商
- 亞太地區市場規模與預測（按國家）
- 亞太地區市場規模與預測（依管理途徑）
- 亞太地區市場規模與預測（按治療類型）
- 亞太地區市場規模和預測（按最終用戶）
- 印度
- 中國
- 日本
- 韓國
- 澳洲
- 泰國
- 印尼
- 菲律賓
- 亞太地區其他地區
拉丁美洲
- 概述
- 拉丁美洲龐貝氏症主要製造商
- 拉丁美洲市場規模與預測（按國家）
- 拉丁美洲市場規模與預測（按管理途徑）
- 拉丁美洲市場規模與預測（按治療類型）
- 拉丁美洲市場規模和預測（按最終用戶）
- 巴西
- 墨西哥
- 阿根廷
- 哥倫比亞
- 拉丁美洲其他地區
中東和非洲
- 概述
- 中東和非洲龐貝病主要製造商
- 中東和非洲市場規模及預測（按國家）
- 中東和非洲市場規模及預測（按管理途徑）
- 中東和非洲市場規模及預測（按治療類型）
- 中東和非洲市場規模和預測（按最終用戶）
- 沙烏地阿拉伯
- 阿拉伯聯合大公國
- 以色列
- 土耳其
- 阿爾及利亞
- 埃及
- MEA 的其餘部分

第 11 章：主要供應商分析 - 龐貝氏症產業

競爭儀表板
公司簡介
- Sanofi Genzyme
- Amicus Therapeutics
- BioMarin Pharmaceutical
- Ultragenyx Pharmaceutical
- Audentes Therapeutics
- Avrobio
- Regenxbio
- EpiVax
- Selecta Biosciences
- Cytokinetics
- Adverum Biotechnologies
- Audentes Therapeutics
- JCR Pharmaceuticals
- Audentes Therapeutics
- Valerion Therapeutics

第 12 章：360 度分析師視角

第 13 章：附錄

研究方法論
參考
縮寫
免責聲明
聯絡我們

簡介目錄圖表

Product Code: ANV1642

REPORT HIGHLIGHT

Pompe Disease Market size was valued at USD 1,322.23 Million in 2022, expanding at a CAGR of 4.2% from 2023 to 2030.

Pompe disease, a rare genetic disorder, arises from a deficiency of the enzyme acid alpha-glucosidase (GAA). This deficiency leads to the accumulation of glycogen within cells, with the most pronounced impact on muscle tissues, resulting in a gradual loss of function. Symptoms commonly associated with this condition encompass muscle weakness, respiratory challenges, and cardiac complications. The disease's severity varies, with some individuals experiencing early-onset forms that can have life-threatening cardiac and muscular consequences, while others may have a later onset characterized primarily by muscle weakening. Pompe disease underscores the crucial importance of early detection and ongoing medical management to mitigate its impact on an individual's overall quality of life.

Pompe Disease Market - Market Dynamics:

Growing collaboration between pharmaceutical companies, research institutions, and patient advocacy groups to propel market demand

The advancement of research and treatment for Pompe disease is significantly propelled by the increasing collaboration among pharmaceutical companies, academic institutions, and advocacy organizations dedicated to patients with this condition. This collaborative synergy facilitates the exchange of knowledge, expertise, and resources, thereby expediting the discovery of innovative therapies. Regulatory bodies provide incentives and orphan drug designations to incentivize companies to invest in rare disease research. Additionally, patient advocacy groups play a pivotal role by raising public awareness and organizing fundraising initiatives that generate funds for research and clinical trials. This collective endeavor enhances our understanding of the disease's underlying causes and paves the way for the development of personalized treatments, ultimately improving the prognosis and quality of life for individuals affected by Pompe disease.

Pompe Disease Market - Key Insights:

Our research analyst estimates that the global Pompe Disease market is poised for annual growth at a CAGR of approximately 4.2% during the forecast period from 2023 to 2030. This projected growth is attributed to the increasing collaboration among pharmaceutical firms, research institutions, and patient advocacy groups, indicating a positive trend toward advancing Pompe Disease research and treatment.

The Global Pompe Disease Market is categorized based on various factors, including Route of Administration, End-Use, and Region.

Within the Route of Administration category, Parenteral administration stood out as the dominant segment in the year 2022. This indicates a significant preference for this mode of administration in treating Pompe Disease.

In terms of End-Use segmentation, Hospitals took the lead in 2022. This suggests that hospitals play a crucial role in providing medical care and treatment for Pompe Disease patients.

Moreover, North America emerged as the primary revenue generator in 2022 among different regions.

Pompe Disease Market- Segmentation Analysis:

The Global Pompe Disease Market presents segmentation based on various factors, including Route of Administration, End-Use, Treatment Type, and Region.

Among the categories determined by Route of Administration, the Parenteral sector takes the lead in market dominance. This indicates a prevalent preference for parenteral treatments in managing Pompe disease, a rare genetic disorder. The administration of enzyme replacement therapy (ERT) through intravenous injections plays a pivotal role in disease management. This therapy directly delivers the deficient enzyme, effectively addressing glycogen accumulation within cells, and thereby improving muscle function in affected individuals.

Pompe Disease Market- Competitive Landscape:

The landscape of Pompe disease research and treatment is characterized by a dynamic interplay among pharmaceutical companies, research institutions, and advocacy groups. Collaborative efforts with academic organizations foster scientific advancements, while patient advocacy groups play a pivotal role in raising awareness, funding research endeavors, and advocating for regulatory support. The orphan drug designation further incentivizes competitiveness within the field. In this competitive environment, companies strive to set themselves apart by emphasizing treatment efficacy, accessibility, and the implementation of patient support initiatives. This competition acts as a catalyst for accelerated progress, leading to a broader range of therapeutic options and an overall enhancement in the quality of care provided to individuals with Pompe disease.

Recent Developments:

In June 2023, Amicus Therapeutics, a globally oriented biotechnology firm with a patient-centered approach, specializing in the development and commercialization of innovative medications for rare diseases, announced a significant milestone. The European Commission (EC) granted approval for Opfolda (miglustat) 65mg capsules, an enzyme stabilizer for cipaglucosidase alfa, as a long-term enzyme replacement therapy for adults afflicted with late-onset Pompe disease.

SCOPE OF THE REPORT

The scope of this report covers the market by its major segments, which include as follows:

GLOBAL POMPE DISEASE MARKET KEY PLAYERS

Sanofi Genzyme
Amicus Therapeutics
BioMarin Pharmaceutical
Ultragenyx Pharmaceutical
Audentes Therapeutics
Avrobio
Regenxbio
EpiVax
Selecta Biosciences
Cytokinetics
Adverum Biotechnologies
Audentes Therapeutics
JCR Pharmaceuticals
Audentes Therapeutics
Valerion Therapeutics

GLOBAL POMPE DISEASE MARKET, BY ROUTE OF ADMINISTRATION

Oral
Parenteral

GLOBAL POMPE DISEASE MARKET, BY END-USE

Hospitals
Ambulatory Surgical Centers
Other

GLOBAL POMPE DISEASE MARKET, BY TREATMENT TYPE

Substrate Reduction Therapy (SRT)
Enzyme Replacement Therapy (ERT)
Other

GLOBAL POMPE DISEASE MARKET, BY REGION

North America

The U.S.
Canada

Europe

Germany
France
Italy
Spain
United Kingdom
Russia
Netherlands
Sweden
Poland
Rest of Europe

Asia Pacific

India
China
South Korea
Japan
Australia
Thailand
Indonesia
Philippines
Rest of APAC

Latin America

Brazil
Mexico
Argentina
Colombia
Rest of LATAM

The Middle East and Africa

Saudi Arabia
United Arab Emirates
Israel
Turkey
Algeria
Egypt
Rest of MEA

1. Pompe Disease Market Overview

1.1. Study Scope
1.2. Market Estimation Years

2. Executive Summary

2.1. Market Snippet
- 2.1.1. Pompe Disease Market Snippet by Route of Administration
- 2.1.2. Pompe Disease Market Snippet by Treatment Type
- 2.1.3. Pompe Disease Market Snippet by End-User
- 2.1.4. Pompe Disease Market Snippet by Country
- 2.1.5. Pompe Disease Market Snippet by Region
2.2. Competitive Insights

3. Pompe Disease Key Market Trends

3.1. Pompe Disease Market Drivers
- 3.1.1. Impact Analysis of Market Drivers
3.2. Pompe Disease Market Restraints
- 3.2.1. Impact Analysis of Market Restraints
3.3. Pompe Disease Market Opportunities
3.4. Pompe Disease Market Future Trends

4. Pompe Disease Industry Study

4.1. PEST Analysis
4.2. Porter's Five Forces Analysis
4.3. Growth Prospect Mapping
4.4. Regulatory Framework Analysis

5. Pompe Disease Market: COVID-19 Impact Analysis

5.1. Pre-COVID-19 Impact Analysis
5.2. Post-COVID-19 Impact Analysis
- 5.2.1. Top Performing Segments
- 5.2.2. Marginal Growth Segments
- 5.2.3. Top Looser Segments
- 5.2.4. Marginal Loss Segments

6. Pompe Disease Market Landscape

6.1. Pompe Disease Market Share Analysis, 2022
6.2. Breakdown Data, by Key Manufacturer
- 6.2.1. Established Players' Analysis
- 6.2.2. Emerging Players' Analysis

7. Pompe Disease Market - By Route of Administration

7.1. Overview
- 7.1.1. Segment Share Analysis, By Route of Administration, 2022 & 2030 (%)
- 7.1.2. Oral
- 7.1.3. Parenteral

8. Pompe Disease Market - By Treatment Type

8.1. Overview
- 8.1.1. Segment Share Analysis, By Treatment Type, 2022 & 2030 (%)
- 8.1.2. Substrate Reduction Therapy (SRT)
- 8.1.3. Enzyme Replacement Therapy (ERT)
- 8.1.4. Other

9. Pompe Disease Market - By End-User

9.1. Overview
- 9.1.1. Segment Share Analysis, By End-User, 2022 & 2030 (%)
- 9.1.2. Hospitals
- 9.1.3. Ambulatory Surgical Centers
- 9.1.4. Other

10. Pompe Disease Market- By Geography

10.1. Introduction
- 10.1.1. Segment Share Analysis, By Geography, 2022 & 2030 (%)
10.2. North America
- 10.2.1. Overview
- 10.2.2. Pompe Disease Key Manufacturers in North America
- 10.2.3. North America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
- 10.2.4. North America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
- 10.2.5. North America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
- 10.2.6. North America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.2.7. U.S.
  - 10.2.7.1. Overview
  - 10.2.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.2.7.3. U.S. Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.2.7.4. U.S. Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.2.7.5. U.S. Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.2.8. Canada
  - 10.2.8.1. Overview
  - 10.2.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.2.8.3. Canada Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.2.8.4. Canada Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.2.8.5. Canada Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
10.3. Europe
- 10.3.1. Overview
- 10.3.2. Pompe Disease Key Manufacturers in Europe
- 10.3.3. Europe Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
- 10.3.4. Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
- 10.3.5. Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
- 10.3.6. Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.7. Germany
  - 10.3.7.1. Overview
  - 10.3.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.7.3. Germany Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.7.4. Germany Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.7.5. Germany Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.8. Italy
  - 10.3.8.1. Overview
  - 10.3.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.8.3. Italy Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.8.4. Italy Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.8.5. Italy Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.9. United Kingdom
  - 10.3.9.1. Overview
  - 10.3.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.9.3. United Kingdom Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.9.4. United Kingdom Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.9.5. United Kingdom Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.10. France
  - 10.3.10.1. Overview
  - 10.3.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.10.3. France Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.10.4. France Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.10.5. France Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.11. Russia
  - 10.3.11.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.11.2. Russia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.11.3. Russia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.11.4. Russia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.12. Netherlands
  - 10.3.12.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.12.2. Netherlands Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.12.3. Netherlands Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.12.4. Netherlands Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.13. Sweden
  - 10.3.13.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.13.2. Sweden Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.13.3. Sweden Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.13.4. Sweden Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.14. Poland
  - 10.3.14.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.14.2. Poland Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.14.3. Poland Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.14.4. Poland Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.3.15. Rest of Europe
  - 10.3.15.1. Overview
  - 10.3.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.3.15.3. Rest of the Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.3.15.4. Rest of the Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.3.15.5. Rest of the Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
10.4. Asia Pacific (APAC)
- 10.4.1. Overview
- 10.4.2. Pompe Disease Key Manufacturers in Asia Pacific
- 10.4.3. Asia Pacific Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
- 10.4.4. Asia Pacific Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
- 10.4.5. Asia Pacific Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
- 10.4.6. Asia Pacific Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.7. India
  - 10.4.7.1. Overview
  - 10.4.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.7.3. India Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.7.4. India Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.7.5. India Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.8. China
  - 10.4.8.1. Overview
  - 10.4.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.8.3. China Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.8.4. China Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.8.5. China Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.9. Japan
  - 10.4.9.1. Overview
  - 10.4.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.9.3. Japan Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.9.4. Japan Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.9.5. Japan Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.10. South Korea
  - 10.4.10.1. Overview
  - 10.4.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.10.3. South Korea Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.10.4. South Korea Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.10.5. South Korea Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.11. Australia
  - 10.4.11.1. Overview
  - 10.4.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.11.3. Australia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.11.4. Australia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.11.5. Australia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.12. Thailand
  - 10.4.12.1. Overview
  - 10.4.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.12.3. Thailand Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.12.4. Thailand Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.12.5. Thailand Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.13. Indonesia
  - 10.4.13.1. Overview
  - 10.4.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.13.3. Indonesia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.13.4. Indonesia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.13.5. Indonesia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.14. Philippines
  - 10.4.14.1. Overview
  - 10.4.14.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.14.3. Philippines Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.14.4. Philippines Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.14.5. Philippines Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.4.15. Rest of APAC
  - 10.4.15.1. Overview
  - 10.4.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.4.15.3. Rest of APAC Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.4.15.4. Rest of APAC Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.4.15.5. Rest of APAC Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
10.5. Latin America
- 10.5.1. Overview
- 10.5.2. Pompe Disease Key Manufacturers in Latin America
- 10.5.3. Latin America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
- 10.5.4. Latin America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
- 10.5.5. Latin America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
- 10.5.6. Latin America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.5.7. Brazil
  - 10.5.7.1. Overview
  - 10.5.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.5.7.3. Brazil Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.5.7.4. Brazil Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.5.7.5. Brazil Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.5.8. Mexico
  - 10.5.8.1. Overview
  - 10.5.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.5.8.3. Mexico Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.5.8.4. Mexico Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.5.8.5. Mexico Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.5.9. Argentina
  - 10.5.9.1. Overview
  - 10.5.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.5.9.3. Argentina Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.5.9.4. Argentina Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.5.9.5. Argentina Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.5.10. Colombia
  - 10.5.10.1. Overview
  - 10.5.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.5.10.3. Colombia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.5.10.4. Colombia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.5.10.5. Colombia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.5.11. Rest of LATAM
  - 10.5.11.1. Overview
  - 10.5.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.5.11.3. Rest of LATAM Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.5.11.4. Rest of LATAM Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.5.11.5. Rest of LATAM Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
10.6. Middle East and Africa
- 10.6.1. Overview
- 10.6.2. Pompe Disease Key Manufacturers in Middle East and Africa
- 10.6.3. Middle East and Africa Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
- 10.6.4. Middle East and Africa Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
- 10.6.5. Middle East and Africa Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
- 10.6.6. Middle East and Africa Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.7. Saudi Arabia
  - 10.6.7.1. Overview
  - 10.6.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.7.3. Saudi Arabia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.7.4. Saudi Arabia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.7.5. Saudi Arabia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.8. United Arab Emirates
  - 10.6.8.1. Overview
  - 10.6.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.8.3. United Arab Emirates Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.8.4. United Arab Emirates Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.8.5. United Arab Emirates Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.9. Israel
  - 10.6.9.1. Overview
  - 10.6.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.9.3. Israel Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.9.4. Israel Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.9.5. Israel Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.10. Turkey
  - 10.6.10.1. Overview
  - 10.6.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.10.3. Turkey Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.10.4. Turkey Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.10.5. Turkey Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.11. Algeria
  - 10.6.11.1. Overview
  - 10.6.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.11.3. Algeria Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.11.4. Algeria Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.11.5. Algeria Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.12. Egypt
  - 10.6.12.1. Overview
  - 10.6.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.12.3. Egypt Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.12.4. Egypt Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.12.5. Egypt Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
- 10.6.13. Rest of MEA
  - 10.6.13.1. Overview
  - 10.6.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
  - 10.6.13.3. Rest of MEA Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
  - 10.6.13.4. Rest of MEA Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
  - 10.6.13.5. Rest of MEA Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)

11. Key Vendor Analysis- Pompe Disease Industry

11.1. Competitive Dashboard
11.2. Company Profiles
- 11.2.1. Sanofi Genzyme
- 11.2.2. Amicus Therapeutics
- 11.2.3. BioMarin Pharmaceutical
- 11.2.4. Ultragenyx Pharmaceutical
- 11.2.5. Audentes Therapeutics
- 11.2.6. Avrobio
- 11.2.7. Regenxbio
- 11.2.8. EpiVax
- 11.2.9. Selecta Biosciences
- 11.2.10. Cytokinetics
- 11.2.11. Adverum Biotechnologies
- 11.2.12. Audentes Therapeutics
- 11.2.13. JCR Pharmaceuticals
- 11.2.14. Audentes Therapeutics
- 11.2.15. Valerion Therapeutics

12. 360 Degree Analyst View

13. Appendix

13.1. Research Methodology
13.2. References
13.3. Abbreviations
13.4. Disclaimer
13.5. Contact Us

簡介目錄圖表

List of Tables

TABLE List of data sources
TABLE Market drivers; Impact Analysis
TABLE Market restraints; Impact Analysis
TABLE Pompe Disease Market: Route of Administration Snapshot (2022)
TABLE Segment Dashboard; Definition and Scope, by Route of Administration
TABLE Global Pompe Disease Market, by Route of Administration 2018-2030 (USD Million)
TABLE Pompe Disease Market: Treatment Type Snapshot (2022)
TABLE Segment Dashboard; Definition and Scope, by Treatment Type
TABLE Global Pompe Disease Market, by Treatment Type 2018-2030 (USD Million)
TABLE Pompe Disease Market: End-User Snapshot (2022)
TABLE Segment Dashboard; Definition and Scope, by End-User
TABLE Global Pompe Disease Market, by End-User 2018-2030 (USD Million)
TABLE Pompe Disease Market: Regional snapshot (2022)
TABLE Segment Dashboard; Definition and Scope, by Region
TABLE Global Pompe Disease Market, by Region 2018-2030 (USD Million)
TABLE North America Pompe Disease Market, by Country, 2018-2030 (USD Million)
TABLE North America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
TABLE North America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
TABLE North America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
TABLE Europe Pompe Disease Market, by Country, 2018-2030 (USD Million)
TABLE Europe Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
TABLE Europe Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
TABLE Europe Pompe Disease Market, by End-User, 2018-2030 (USD Million)
TABLE Asia Pacific Pompe Disease Market, by Country, 2018-2030 (USD Million)
TABLE Asia Pacific Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
TABLE Asia Pacific Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
TABLE Asia Pacific Pompe Disease Market, by End-User, 2018-2030 (USD Million)
TABLE Latin America Pompe Disease Market, by Country, 2018-2030 (USD Million)
TABLE Latin America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
TABLE Latin America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
TABLE Latin America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
TABLE Middle East and Africa Pompe Disease Market, by Country, 2018-2030 (USD Million)
TABLE Middle East and Africa Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
TABLE Middle East and Africa Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
TABLE Middle East and Africa Pompe Disease Market, by End-User, 2018-2030 (USD Million)