市場調查報告書
商品編碼
1422966
2024-2032 年龐貝氏症治療市場(依治療方法、給藥途徑、配銷通路、適應症類型和地區)Pompe Disease Treatment Market by Treatment, Route of Administration, Distribution Channel, Indication Type, and Region 2024-2032 |
2023年,全球龐貝氏症治療市場規模達到10億美元。展望未來, IMARC Group預計到2032年市場規模將達到13億美元,2024-2032年複合年成長率(CAGR)為2.58%。臨床研究和試驗數量的增加、ERT 的日益普及以及患有龐貝病的患者數量的增加是推動市場發展的一些關鍵因素。
龐貝氏症是一種遺傳性疾病,由身體細胞中一種稱為肝醣的複合糖積聚引起,會影響器官、組織和肌肉。它是由溶酶體酶酸性α-葡萄糖苷酶(GAA)缺乏引起的常染色體隱性肝醣儲存症候群。它與肌肉無力、肝臟腫大、呼吸困難、聽力問題、肺部感染、心律不整和體重減輕有關。可使用各種工具和測試進行診斷,包括肌電圖、X 光和磁振造影 (MRI)。龐貝氏症可以透過藥物、酵素替代療法 (ERT)、底物減少療法 (SRT)、伴侶高級替代療法 (CART) 和注射來治療,有助於改善生活品質。
個體中遺傳異常的盛行率顯著上升,患有龐貝氏症的患者數量也隨之增加。再加上嬰兒龐貝氏症的增加以及父母對新生兒健康的日益擔憂,這是推動市場成長的關鍵因素之一。此外,越來越多的老年人口容易患上這些疾病,導致對龐貝氏症治療的需求不斷增加。此外,開發龐貝氏症新療法的臨床研究和試驗數量不斷增加,正在對市場產生正面影響。除此之外,人們對 ERT 治療龐貝氏症的認知不斷提高,有利於市場的成長。此外,人們對各種治療方法的認知有所提高,包括幹細胞移植、骨髓移植、化療和免疫療法,因為它們具有眾多優點。再加上人們對 Lumizyme 等 ERT 治療替代品易於獲得的認知,正在為市場創造積極的前景。除此之外,擴大採用健康保險政策,為龐貝氏症治療提供財政援助並最大限度地減少醫療支出。此外,許多國家的政府和非政府組織 (NGO) 正在採取措施,為所有人提供優質的醫療保健設施。加上診斷技術的顯著改進,預計將為市場帶來良好的前景。
The global Pompe disease treatment market size reached US$ 1.0 Billion in 2023. Looking forward, IMARC Group expects the market to reach US$ 1.3 Billion by 2032, exhibiting a growth rate (CAGR) of 2.58% during 2024-2032. The increasing number of clinical studies and trials, the rising popularity of ERT, and the growing number of patients suffering from Pompe disease represent some of the key factors driving the market.
Pompe disease is a genetic disorder caused by the buildup of a complex sugar known as glycogen in the cells of the body, which affects organs, tissues, and muscles. It is an autosomal recessive glycogen storage syndrome caused by the deficiency of lysosomal enzyme acid a-glucosidase (GAA). It is associated with weak muscles, enlarged liver, trouble breathing, hearing problem, lung infection, irregular heartbeat, and losing weight. It is diagnosed using various tools and tests, including electromyography, X-rays, and magnetic resonance imaging (MRI). Pompe disease can be treated using medications, enzyme replacement therapy (ERT), substrate reduction therapy (SRT), chaperone-advanced replacement therapy (CART), and injections, which aid in improving the quality of life.
There is a considerable rise in the prevalence of genetic abnormalities among individuals and an increase in the number of patients suffering from Pompe disease. This, coupled with the growing Pompe disease among infants and increasing concerns among parents about the health of their newborns, represents one of the key factors bolstering the growth of the market. Moreover, the growing geriatric population that is susceptible to developing these medical disorders is resulting in an increasing demand for Pompe disease treatment. In addition, the expanding number of clinical studies and trials to develop new treatments for Pompe disease is influencing the market positively. Apart from this, the rising awareness among people about ERT for curing Pompe disease is favoring the market growth. Furthermore, there is an increase in awareness about various treatments, including stem cell transplant, bone marrow transplantation, chemotherapy, and immunotherapy, on account of their numerous advantages. This, along with the awareness about the easy availability of ERT treatment alternatives like lumizyme, is creating a positive outlook for the market. Besides this, there is a rise in the adoption of health insurance policies that provide financial assistance and minimize healthcare expenditure for Pompe disease treatment. Additionally, governments and non-governmental organizations (NGOs) of numerous countries are undertaking measures to offer quality healthcare facilities that are accessible to all. This, along with significant improvements in the diagnostic technologies, is anticipated to provide a favorable outlook to the market.
IMARC Group provides an analysis of the key trends in each segment of the global Pompe disease treatment market, along with forecasts at the global, regional, and country level from 2024-2032. Our report has categorized the market based on treatment, route of administration, distribution channel, and indication type.
Enzyme Replacement Therapy (ERT)
Substrate Reduction Therapy (SRT)
Chaperone-Advanced Replacement Therapy (CART)
Others
The report has provided a detailed breakup and analysis of the Pompe disease treatment market based on the treatment. This includes enzyme replacement therapy (ERT), substrate reduction therapy (SRT), chaperone-advanced replacement therapy (CART), and others. According to the report, enzyme replacement therapy (ERT) represented the largest segment.
Oral
Intravenous
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the route of administration has also been provided in the report. This includes oral, intravenous, and others.
Hospital and Clinics Pharmacies
Retail Pharmacies
Online Pharmacies
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the distribution channel has also been provided in the report. This includes hospital and clinics, retail, and online pharmacies, and others. According to the report, hospital and clinics pharmacies accounted for the largest market share.
Infantile-Onset Pompe Disease (IOPD)
Classic Infantile Form
Non-Classic Infantile Form
Late-Onset Pompe Disease (LOPD)
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the indication type has also been provided in the report. This includes infantile-onset Pompe disease (IOPD), classic infantile form, non-classic infantile form, late-onset Pompe disease (LOPD), and others. According to the report, late-onset Pompe disease (LOPD) accounted for the largest market share.
North America
United States
Canada
Asia Pacific
China
Japan
India
South Korea
Australia
Indonesia
Others
Europe
Germany
France
United Kingdom
Italy
Spain
Russia
Others
Latin America
Brazil
Mexico
Others
Middle East and Africa
The report has also provided a comprehensive analysis of all the major regional markets that include North America (the United States and Canada), Asia Pacific (China, Japan, India, South Korea, Australia, Indonesia, and others), Europe (Germany, France, the United Kingdom, Italy, Spain, Russia, and others), Latin America (Brazil, Mexico, and others), and the Middle East and Africa. According to the report, North America was the largest market for Pompe disease treatment. Some of the factors driving the North America Pompe disease treatment market included the growing awareness about various alternative treatments, increasing number of clinical studies and trials, and well-established healthcare facilities.
The report has also provided a comprehensive analysis of the competitive landscape in the global Pompe disease treatment market. Detailed profiles of all major companies have also been provided. Some of the companies covered include Amicus Therapeutics Inc., Audentes Therapeutics Inc. (Astellas US Holding Inc.), Oxyrane UK Limited, Sanofi S.A., Spark Therapeutics Inc, etc.
Kindly, note that this only represents a partial list of companies, and the complete list has been provided in the report