市場調查報告書
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1464907
Duchenne氏肌肉失養症治療藥物市場:按藥物類型、給藥方法和最終用途分類 - 全球預測 2024-2030Duchenne Muscular Dystrophy Drugs Market by Drug Type (Casimersen, Deflazacort, Delandistrogene Moxeparvovec), Administration Method (Oral, Parental), End-Use - Global Forecast 2024-2030 |
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Duchenne氏肌肉失養症治療藥物市場規模預計2023年為15.7億美元,預計2024年將達17億美元,2030年將達28億美元,複合年成長率為8.61%。
Duchenne氏肌肉失養症(DMD) 治療市場專注於專門用於治療 DMD 的藥品的銷售、開拓和生產,DMD 是一種以進行性肌肉退化和肌無力為特徵的遺傳性疾病。基因研究的進步和對 DMD 基因基礎了解的突破正在帶來更有針對性和更有效的治療方法,有助於市場擴張。全球醫療保健支出的增加正在改善 DMD 治療的可近性並有助於市場擴張。政府和非營利組織的資金和舉措正在支持研究和開發工作,並促進將 DMD 治療引入市場。對藥物核准和市場引入的嚴格監管要求可能會延遲獲得創新療法的機會,並且是市場領域的一個挑戰。此外,基因編輯技術的進步,如CRISPR/Cas9和其他基因編輯工具,為Duchenne氏肌肉失養症的治療提供了可能性。根據個人基因譜量身定做的個人化醫療方法的開發有可能提高療效並最大限度地減少副作用,從而為市場成長創造機會。
主要市場統計 | |
---|---|
基準年[2023] | 15.7億美元 |
預測年份 [2024] | 17億美元 |
預測年份 [2030] | 28億美元 |
複合年成長率(%) | 8.61% |
藥物類型:卡西默森擴大被偏好作為Duchenne氏肌肉失養症的標靶治療
Casimersen 被核准用於治療已確診的外顯子 45 跳躍突變的 DMD 患者。這種基於需求的卡迪默森偏好對於具有某些遺傳傾向的患者至關重要,並提供了標靶治療選擇。無論特定的基因突變如何,地夫可特都能有效減緩 DMD 的進展並提高廣大患者的肌肉力量。 Derandystrogen moxeparvovec (Roctavian) 基因療法的目標患者是那些將從直接糾正導致 DMD 的基因缺陷的方法中受益的患者。 Eteplirsen (exondis51) 適用於因外顯子 51 跳躍而確認 DMD 基因突變的 DMD 患者。 Golodirsen 滿足小眾病患小組的需求,並針對外顯子 53 跳躍的特定基因突變提供標靶基因治療。 Viltolarsen 被核准用於治療外顯子 53 跳躍的 DMD 患者,透過針對特定基因突變為受影響的患者提供精準醫療方法。
最終用途:門診 DMD 治療的採用率增加
門診中心,也稱為流動護理中心,為不需要住院的患者提供醫療服務。門診中心因其便利性和成本效益而日益成為 DMD 等慢性疾病的常規檢查、診斷和治療的首選。居家照護設施是一個快速發展的領域,可滿足患者在自己家中接受醫療保健服務的願望,包括 DMD 藥物治療。居家照護在患者舒適的家中提供持續、個人化的 DMD 藥物治療和管理。
區域洞察
美國和加拿大是參與Duchenne氏肌肉失養症(DMD) 治療藥物開發的主要企業的重要區域。美洲地區的特點是消費者意識高、研發投入高、政府政策優惠。美國在突破性治療方法的開發中佔據關鍵地位,並已為創新的 DMD治療方法申請了多項專利。加拿大展現了強而有力的政府支持和官民合作關係來促進市場成長。歐盟 (EU) 國家一直處於 DMD 藥物開發監管支持的最前沿,並採取了多項舉措來支持研究和獲得治療。歐洲、中東和非洲地區的專利活動非常活躍,多個國家都對發現做出了貢獻。中東地區市場規模雖小,但投資不斷加大,認可度不斷提高。非洲在醫療保健基礎設施和治療取得方面面臨挑戰,並透過國際夥伴關係和投資提供成長潛力。亞太地區,特別是中國、日本和印度,DMD 治療市場正在顯著成長。亞太地區國家的市場成長歸功於意識的提高、政府措施和醫療基礎設施的改善。亞太地區國家的研究和投資十分活躍,其中日本在創新治療方法和專利申請方面處於領先地位。中國和印度正在迅速推進研究並提供具有成本效益的治療方法,顯著影響市場動態和客戶購買行為。
FPNV定位矩陣
FPNV定位矩陣對於評估Duchenne氏肌肉失養症藥物市場至關重要。我們檢視與業務策略和產品滿意度相關的關鍵指標,以對供應商進行全面評估。這種深入的分析使用戶能夠根據自己的要求做出明智的決策。根據評估,供應商被分為四個成功程度不同的像限:前沿(F)、探路者(P)、利基(N)和重要(V)。
市場佔有率分析
市場佔有率分析是一種綜合工具,可以對Duchenne氏肌肉失養症治療藥物市場供應商的現狀進行深入而深入的研究。全面比較和分析供應商在整體收益、基本客群和其他關鍵指標方面的貢獻,以便更好地了解公司的績效及其在爭奪市場佔有率時面臨的挑戰。此外,該分析還提供了對該行業競爭特徵的寶貴見解,包括在研究基準年觀察到的累積、分散主導地位和合併特徵等因素。詳細程度的提高使供應商能夠做出更明智的決策並制定有效的策略,以獲得市場競爭優勢。
1. 市場滲透率:提供有關主要企業所服務的市場的全面資訊。
2. 市場開拓:我們深入研究利潤豐厚的新興市場,並分析其在成熟細分市場的滲透率。
3. 市場多元化:提供有關新產品發布、開拓地區、最新發展和投資的詳細資訊。
4. 競爭評估和情報:對主要企業的市場佔有率、策略、產品、認證、監管狀況、專利狀況和製造能力進行全面評估。
5. 產品開發與創新:提供對未來技術、研發活動和突破性產品開發的見解。
1.Duchenne氏肌肉失養症治療藥物市場規模及預測是多少?
2.Duchenne氏肌肉失養症治療藥物市場預測期內需要考慮投資的產品、細分市場、應用和領域有哪些?
3.Duchenne氏肌肉失養症治療藥物市場的技術趨勢和法規結構是什麼?
4.Duchenne氏肌肉失養症治療藥物市場主要供應商的市場佔有率是多少?
5. 進入Duchenne氏肌肉失養症藥物市場的合適型態和策略手段是什麼?
[182 Pages Report] The Duchenne Muscular Dystrophy Drugs Market size was estimated at USD 1.57 billion in 2023 and expected to reach USD 1.70 billion in 2024, at a CAGR 8.61% to reach USD 2.80 billion by 2030.
The Duchenne muscular dystrophy (DMD) drugs market focuses on the sales, development, and production of pharmaceuticals specifically aimed at treating DMD, a genetic disorder characterized by progressive muscle degeneration and weakness. Advancements in genetic research and breakthroughs in understanding the genetic basis of DMD are leading to more targeted and effective treatments, contributing to the market expansion. Higher global healthcare expenditure enables better treatment access for DMD, contributing to market growth. Funding and initiatives by governments and non-profit organizations boost research and development efforts, enhancing the market adoption of DMD drugs. Stringent regulatory requirements for drug approval and market introduction may delay access to innovative treatments, posing challenges in the market space. Moreover, ongoing advancements in gene editing technologies such as CRISPR/Cas9 and other gene-editing tools offer potential for curative treatments of Duchenne muscular dystrophy. The development of personalized medicine approaches tailored to individual genetic profiles may improve efficacy and minimize side effects, generating opportunities for market growth.
KEY MARKET STATISTICS | |
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Base Year [2023] | USD 1.57 billion |
Estimated Year [2024] | USD 1.70 billion |
Forecast Year [2030] | USD 2.80 billion |
CAGR (%) | 8.61% |
Drug Type: Rising preference for casimersen for targeted treatment of Duchenne muscular dystrophy
Casimersen is approved for treating DMD in patients with a confirmed mutation due to exon 45 skipping. This need-based preference for casimersen is critical for patients with a specific genetic makeup, providing a targeted treatment option. Deflazacort ensures efficacy in delaying disease progression and improving muscle strength to slow the progression of DMD across a broad range of patients, regardless of their specific genetic mutation. Delandistrogene Moxeparvovec (Roctavian) gene therapy is designed for patients that benefit from a direct approach to correcting the gene defect responsible for DMD. Eteplirsen (Exondys 51) is preferred for DMD patients observing confirmed mutation of the DMD gene due to exon 51 skipping. Golodirsen meets the needs of a niche patient group, offering a targeted genetic treatment with a specific genetic mutation amenable to exon 53 skipping. Viltolarsen is approved for DMD patients amenable to exon 53 skipping that targets a specific genetic alteration, providing a precision medicine approach for affected patients.
End-Use: Increasing adoption of DMD drugs in ambulatory centers
Ambulatory centers, also known as outpatient care centers, provide medical services to patients that do not require hospital admission. Ambulatory center facilities have been increasingly preferred for routine check-ups, diagnosis, and the management of chronic conditions such as DMD due to their convenience and cost-effectiveness. Homecare settings represent a rapidly growing segment that caters to the preference for receiving healthcare services, including DMD drug treatments, in the patient's home. Homecare settings allow for continuous, personalized care and the administration of DMD medications in the comfort of the patient's home.
Regional Insights
In the Americas region, the United States and Canada are pivotal due to the strong presence of key players engaged in developing Duchenne Muscular Dystrophy (DMD) drugs. The Americas region is characterized by high consumer awareness, substantial investments in R&D, and favorable government policies. The United States holds a key position in developing breakthrough therapies and has several patents filed for innovative DMD treatments. Canada demonstrates strong governmental support and public-private partnerships, fostering growth in the market arena. The European Union countries are at the forefront regarding regulatory support for DMD drug development and have several initiatives supporting research and access to treatment. Patent activity is high in the EMEA region, with several countries contributing to discoveries. The Middle East region, although smaller in terms of market size, is witnessing increased investment and growing awareness. Africa faces challenges related to healthcare infrastructure and treatment access and shows potential for growth through international partnerships and investments. The Asia Pacific region, especially China, Japan, and India, has grown significantly in the DMD drugs market. The market growth in the APAC countries is attributed to increasing awareness, governmental initiatives, and improving healthcare infrastructure. Research and investment in APAC countries have been robust, with Japan leading in innovative therapies and patent filings. China and India are rapidly advancing in research and offering cost-effective treatments, significantly affecting market dynamics and customer purchasing behaviors.
FPNV Positioning Matrix
The FPNV Positioning Matrix is pivotal in evaluating the Duchenne Muscular Dystrophy Drugs Market. It offers a comprehensive assessment of vendors, examining key metrics related to Business Strategy and Product Satisfaction. This in-depth analysis empowers users to make well-informed decisions aligned with their requirements. Based on the evaluation, the vendors are then categorized into four distinct quadrants representing varying levels of success: Forefront (F), Pathfinder (P), Niche (N), or Vital (V).
Market Share Analysis
The Market Share Analysis is a comprehensive tool that provides an insightful and in-depth examination of the current state of vendors in the Duchenne Muscular Dystrophy Drugs Market. By meticulously comparing and analyzing vendor contributions in terms of overall revenue, customer base, and other key metrics, we can offer companies a greater understanding of their performance and the challenges they face when competing for market share. Additionally, this analysis provides valuable insights into the competitive nature of the sector, including factors such as accumulation, fragmentation dominance, and amalgamation traits observed over the base year period studied. With this expanded level of detail, vendors can make more informed decisions and devise effective strategies to gain a competitive edge in the market.
Key Company Profiles
The report delves into recent significant developments in the Duchenne Muscular Dystrophy Drugs Market, highlighting leading vendors and their innovative profiles. These include Anuh Pharma Limited, Arlak Biotech Pvt.Ltd., Aurigene Pharmaceutical Services Ltd., Bayer Pharmaceutical, Cipla Inc., Enomark, Glasier Wellness, Inc., GlaxoSmithKline PLC, Johnson & Johnson Services, Inc., Leo Pharma, Lifecare Neuro Products Limited, Mankind Pharma Ltd., Merck & Co., Inc.,, MODASA Pharmaceuticals Pvt. Ltd., Novartis AG, Pfizer Inc., QndQ Derma, RayBiotech, Inc., Ronyd Healthcare Pvt Ltd., Sarepta Therapeutics, Inc., Sumitomo Corporation, Texas Pharmaceuticals Pvt. Ltd., Wallace Pharmaceuticals Pvt Ltd., Wellona Pharma, and Zuventus Healthcare Ltd..
Market Segmentation & Coverage
1. Market Penetration: It presents comprehensive information on the market provided by key players.
2. Market Development: It delves deep into lucrative emerging markets and analyzes the penetration across mature market segments.
3. Market Diversification: It provides detailed information on new product launches, untapped geographic regions, recent developments, and investments.
4. Competitive Assessment & Intelligence: It conducts an exhaustive assessment of market shares, strategies, products, certifications, regulatory approvals, patent landscape, and manufacturing capabilities of the leading players.
5. Product Development & Innovation: It offers intelligent insights on future technologies, R&D activities, and breakthrough product developments.
1. What is the market size and forecast of the Duchenne Muscular Dystrophy Drugs Market?
2. Which products, segments, applications, and areas should one consider investing in over the forecast period in the Duchenne Muscular Dystrophy Drugs Market?
3. What are the technology trends and regulatory frameworks in the Duchenne Muscular Dystrophy Drugs Market?
4. What is the market share of the leading vendors in the Duchenne Muscular Dystrophy Drugs Market?
5. Which modes and strategic moves are suitable for entering the Duchenne Muscular Dystrophy Drugs Market?